Generation and characterization of a ~F508 cystic fibrosis mouse model
Characterization of two rat models of cystic fibrosis—KO and F508del CFTR—Generated by Crispr‐Cas9 - Dreano - 2019 - Animal Models and Experimental Medicine - Wiley Online Library
PDF) Phenotypic Characterization and Comparison of Cystic Fibrosis Rat Models Generated Using CRISPR/Cas9 Gene Editing
Phenotypic Characterization and Comparison of Cystic Fibrosis Rat Models Generated Using CRISPR/Cas9 Gene Editing - The American Journal of Pathology
Highly Efficient Gene Editing of Cystic Fibrosis Patient-Derived Airway Basal Cells Results in Functional CFTR Correction: Molecular Therapy
Characterization of two rat models of cystic fibrosis—KO and F508del CFTR—Generated by Crispr‐Cas9 - Dreano - 2019 - Animal Models and Experimental Medicine - Wiley Online Library
Characterization of two rat models of cystic fibrosis—KO and F508del CFTR—Generated by Crispr‐Cas9 - Dreano - 2019 - Animal Models and Experimental Medicine - Wiley Online Library
Genes | Free Full-Text | Cystic Fibrosis Gene Therapy: Looking Back, Looking Forward | HTML
Rescue of ΔF508-CFTR Trafficking via a GRASP-Dependent Unconventional Secretion Pathway: Cell
Frontiers | Animal Models in the Pathophysiology of Cystic Fibrosis
Characterization of two rat models of cystic fibrosis—KO and F508del CFTR—Generated by Crispr‐Cas9 - Dreano - 2019 - Animal Models and Experimental Medicine - Wiley Online Library
Phenotypic Characterization and Comparison of Cystic Fibrosis Rat Models Generated Using CRISPR/Cas9 Gene Editing - ScienceDirect
ΔF508 in cystic fibrosis: willing but not able | Archives of Disease in Childhood
Frontiers | Bone Cells Differentiation: How CFTR Mutations May Rule the Game of Stem Cells Commitment?
IJMS | Free Full-Text | Unravelling the Regions of Mutant F508del-CFTR More Susceptible to the Action of Four Cystic Fibrosis Correctors | HTML
Frontiers | Adapting Proteostasis and Autophagy for Controlling the Pathogenesis of Cystic Fibrosis Lung Disease
The ΔF508 Mutation Causes CFTR Misprocessing and Cystic Fibrosis–Like Disease in Pigs | Science Translational Medicine
Kcnn4 is a modifier gene of intestinal cystic fibrosis preventing lethality in the Cftr-F508del mouse | Scientific Reports
Frontiers | On the Corner of Models and Cure: Gene Editing in Cystic Fibrosis
Cystic Fibrosis Mouse Models
Phenotypic Characterization and Comparison of Cystic Fibrosis Rat Models Generated Using CRISPR/Cas9 Gene Editing - ScienceDirect
Chemically modified hCFTR mRNAs recuperate lung function in a mouse model of cystic fibrosis | Scientific Reports
In vivo correction of cystic fibrosis mediated by PNA nanoparticles | Science Advances
